FDA approves drug to treat sickle cell disease in patients aged 4 up to 11 years...
Actualidad
Un ensayo aleatorizado de fase 3 de Voxelotor en la enfermedad de células falciformes
Vichinsky E, Hoppe CC, Ataga KI, et al. A Phase 3 Randomized Trial of Voxelotor in Sickle Cell Disease. N Engl J Med. 2019 Aug 8;381(6):509-519. doi: 10.1056/NEJMoa1903212 La...